A Phase I/IIa Safety and Efficacy Study of Nebulized Liposome-mediated Gene Therapy for Cystic Fibrosis Supports a Multidose Trial.

Alton EWFW., Boyd AC., Porteous DJ., Davies G., Davies JC., Griesenbach U., Higgins TE., Gill DR., Hyde SC., Innes JA., UK Cystic Fibrosis Gene Therapy Consortium * None.

DOI

10.1164/rccm.201506-1193LE

Type

Journal article

Journal

Am J Respir Crit Care Med

Publication Date

01/12/2015

Volume

192

Pages

1389 - 1392

Keywords

Administration, Intranasal, Adolescent, Adult, Cystic Fibrosis, Cystic Fibrosis Transmembrane Conductance Regulator, Female, Gene Transfer Techniques, Genetic Therapy, Humans, Liposomes, Male, Middle Aged, Nebulizers and Vaporizers, Young Adult

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